Tag Archives: rare

Just SIX out of every 1 million develop rare heart inflammation after a second dose of vaccine

Just SIX in 1 million people develop rare heart inflammation after a second dose of the Covid vaccine – 85% less than the rate among the unvaccinated, study finds Less than out of every one million people develop myocarditis after the first shot of a Covid vaccine, and around six develop it after the second… Read More »

New extremely rare side effect added to official list for two Covid jabs

A new side effect has been added to the official list for two Covid vaccines by the UK medicines watchdog. Heart inflammation has been linked to both the Pfizer and Moderna jabs in recent weeks after several cases were reported. And the Medicines and Healthcare products Regulatory Agency (MHRA) has now updated the safety information… Read More »

Chiesi Global Rare Diseases Announces FDA Approval of Ferriprox (deferiprone) for Treatment of Transfusional Iron Overload due to Sickle Cell Disease

May 1, 2021 Approval is based on demonstrated reduction in liver iron concentration Expanded indications for patients with sickle cell disease or other anemias, as well as thalassemia – BOSTON, May 1, 2021 /PRNewswire/ — Chiesi Global Rare Diseases, a business unit of Chiesi Farmaceutici S.p.A., an international research-focused healthcare Group (Chiesi Group), announced today… Read More »

Rare Pharmacy Emerges From Specialty, Part 2 – Pharmacy Times

Gordon J. Vanscoy, PharmD, MBA; Pamela Koener, PharmD; and Richard Faris, PhD, RPh Part 1 of this 3-part series, published in last month’s Directions in Oncology Pharmacy™, explored how changes in US federal policy and advances in scientific research have led to the dawn of medical breakthroughs for rare disorders. Part 2 describes how rare… Read More »

Rare ‘Brain Vein’ Strokes Are on the Rise

WEDNESDAY, Aug. 26, 2020 — Most strokes strike when an artery in the brain suddenly becomes blocked, but new research shows a rarer cause of strokes is becoming more common. It’s called cerebral venous thrombosis (CVT), and it happens when a vein in the brain is clogged. While CVT is estimated to cause less than… Read More »

Viltepso (viltolarsen) Injection Granted Accelerated Approval for Rare Duchenne Muscular Dystrophy Mutation

News Consumer News Viltepso (viltolarsen) Injection Granted Accelerated Approval for Rare Duchenne Muscular Dystrophy Mutation THURSDAY, Aug. 13, 2020 — Accelerated approval has been granted to Viltepso (viltolarsen) injection for treatment of patients with Duchenne muscular dystrophy (DMD) and a mutation of the DMD gene amenable to exon 53 skipping, the U.S. Food and Drug… Read More »